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Gene Therapy Research Institution Co. Ltd.
Headquarters:
Kawasaki, Japan
Website:
http://www.en.genetherapy-ri...
Year Founded:
2014
Status:
Private
BioCentury
|
Oct 24, 2024
Product Development
Rare Disease Spotlight: Niemann-Pick pipeline behind two approvals
Therapies aim to enhance lysosomal function to clear cholesterol and glycosphingolipids, mostly via small molecules
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